Additional Campus Affiliations
Associate Professor, Bioengineering
Associate Professor, Biomedical and Translational Sciences
Associate Professor, Carl R. Woese Institute for Genomic Biology
Recent Publications
Miskalis, A., Shirguppe, S., Winter, J., Elias, G., Swami, D., Nambiar, A., Stilger, M., Woods, W. S., Gosstola, N., Gapinske, M., Zeballos, A., Moore, H., Maslov, S., Gaj, T., & Perez-Pinera, P. (2024). SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skipping. Nature communications, 15(1), Article 10354. https://doi.org/10.1038/s41467-024-54529-y
Perez-Pinera, P., & Gaj, T. (2024). Editorial overview: The next-generation of genome editing: The future is now. Current Opinion in Biomedical Engineering, 30, Article 100522. https://doi.org/10.1016/j.cobme.2024.100522
Gapinske, M., Winter, J., Swami, D., Gapinske, L., Woods, W. S., Shirguppe, S., Miskalis, A., Busza, A., Joulani, D., Kao, C. J., Kostan, K., Bigot, A., Bashir, R., & Perez-Pinera, P. (2023). Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors. Molecular Therapy Nucleic Acids, 33, 572-586. https://doi.org/10.1016/j.omtn.2023.07.029
Kim, S., Yuan, J. B., Woods, W. S., Newton, D. A., Perez-Pinera, P., & Song, J. S. (2023). Chromatin structure and context-dependent sequence features control prime editing efficiency. Frontiers in Genetics, 14, Article 1222112. https://doi.org/10.3389/fgene.2023.1222112
Lim, C. K. W., Miskalis, A. J., Perez-Pinera, P., & Gaj, T. (2023). Delivering Base Editors In Vivo by Adeno-Associated Virus Vectors. In Methods in Molecular Biology (pp. 135-158). (Methods in Molecular Biology; Vol. 2606). Humana Press Inc.. https://doi.org/10.1007/978-1-0716-2879-9_11